A recent clinical trial has shown that cellular therapy is safe and effective in stopping the deterioration of upper limb and heart functions in patients with late-stage Duchenne muscular dystrophy. A ...
An experimental RNA therapy from Avidity Biosciences has early clinical trial results showing it reduced by half the expression of a gene at the root of a rare, inherited form of muscular dystrophy ...
Eleven-year-old Brendan McMahon of Chicago was diagnosed with Duchenne muscular dystrophy when he was six. In a very cool move, DePaul men's basketball has signed him to a National Letter of Intent ...
March 11 (Reuters) - Regenxbio said on Wednesday that interim data from a early-to-mid stage study of its experimental gene therapy in patients with Duchenne muscular dystrophy showed continued ...
Cellular therapy offers promise for patients with Duchenne muscular dystrophy (DMD), a rare genetic disorder causing muscle loss, physical impairments. Cellular therapy offers promise for patients ...
Genetic testing can confirm a muscular dystrophy (MD) diagnosis when symptoms and other tests already suggest MD. It also identifies specific gene mutations that can guide targeted treatment. Genetic ...
SEATTLE and MADISON, Wis., Dec 04, 2013 (GLOBE NEWSWIRE via COMTEX) -- The Jain Foundation, a non-profit organization whose mission is to cure muscular dystrophies caused by dysferlin protein ...
A clinical trial at UC Davis Health and six other sites showed that a cellular therapy offers promise for patients with late-stage Duchenne muscular dystrophy (DMD), a rare genetic disorder causing ...
In an awesome display of support, DePaul has signed an 11-year-old with muscular dystophy to a National Letter of Intent for the 2014-15 season. Brandon McMahon was diagnosed with Duchenne muscular ...
The findings were published in the journal, 'The Lancet.' "HOPE-2 is the first clinical trial to test systemic cell therapy in DMD," said Craig McDonald, the trial's national principal investigator ...